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This Month in Muscular Dystrophy
3/23/2015
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Dr. Jerry Mendell Discusses Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular Dystrophy :: March 2015
14:43
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This Month in Muscular Dystrophy
3/06/2015
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Dr. Kevin Flanigan Discusses IRES-Induced Dystrophin as a Potential Therapy for DMD
24:24
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This Month in Muscular Dystrophy
1/27/2015
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Dr. Louise Rodino-Klapac Discusses Dysferlin Overlap Vectors to Restore Function in Dysferlinopathies
12:40
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This Month in Muscular Dystrophy
7/31/2014
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Dr. Scott Harper Discusses RNAi silencing in Limb Girdle Muscular Dystrophy 1A
16:33
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This Month in Muscular Dystrophy
4/30/2014
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Dr. Brian Kaspar Discusses a New Method for Studying ALS, with Potential to Test Therapeutics in Individual Patients
20:44
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This Month in Muscular Dystrophy
11/27/2013
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Dr. Louis Chicoine Discusses the Effect of Plasmapheresis in Removal of AAV Antibodies for Gene Therapy
11:20
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This Month in Muscular Dystrophy
9/10/2013
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Dr. Volker Straub Discusses the Use of Muscle MRI in Muscular Dystrophy
19:07
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This Month in Muscular Dystrophy
7/15/2013
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Dr. Jeff Chamberlain Discusses Gene and Cell Mediated Therapies for Muscular Dystrophy
31:08
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This Month in Muscular Dystrophy
6/24/2013
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Dr. Paul Martin Discusses Galgt2 Gene Therapy for Muscular Dystrophy
20:31
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This Month in Muscular Dystrophy
3/11/2013
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Dr. Louise Rodino-Klapac Discusses Alpha 7 Integrin As A Therapeutic Approach to Muscular Dystrophy
09:37
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This Month in Muscular Dystrophy
1/16/2013
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Dr. James Ervasti Discusses Stability of Therapeutic Forms of Dystrophin :: January 2013
19:08
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This Month in Muscular Dystrophy
12/21/2012
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Dr. Federica Montanaro Discusses New Cardiac Dystrophin Associated Proteins
17:56
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This Month in Muscular Dystrophy
9/25/2012
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Professor Francesco Muntoni Discusses Congenital Muscular Dystrophies
26:30
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This Month in Muscular Dystrophy
7/10/2012
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Dr. Louise Rodino-Klapac Discusses Advances in Dysferlin Gene Therapy
11:03
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This Month in Muscular Dystrophy
5/30/2012
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Dr. Hugh Allen Discusses Cardiomyopathy in Duchenne Muscular Dystrophy
16:01
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This Month in Muscular Dystrophy
4/30/2012
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Dr. Jerry Mendell Discusses Newborn Screening in Duchenne Muscular Dystrophy
19:18
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This Month in Muscular Dystrophy
3/05/2012
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Dr. Thomas Voit Discusses Gamma Sarcoglycan Gene Therapy
17:43
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This Month in Muscular Dystrophy
2/13/2012
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Dr. Burghes Discusses Antisense Oligomer Treatment in an SMA Mouse Model
18:41
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This Month in Muscular Dystrophy
1/05/2012
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Dr. Steve Wilton Discusses Antisense-Induced Exon Skipping
12:54
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This Month in Muscular Dystrophy
12/01/2011
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Dr. Denis Guttridge Discusses NF-kB Therapy for Duchenne Muscular Dystrophy
18:11
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